Reports to: VP, US Medical Affairs & Patient Advocacy

About This Role:

The Senior Director, Medical Affairs, Neuromuscular Team will lead the development and execution of the US medical strategy for givinostat in Duchenne muscular dystrophy. The qualified candidate will serve as a key medical representative in the US, supporting external medical expert engagement and development, communication and evidence generation strategy, and cross-functional collaboration.

What You'll Do: 

• Be responsible for execution of the US Neurometabolic Medical Affairs strategy aligned with corporate objectives and product lifecycle needs. 

• Implement and oversee the execution of US medical plans for Duvyzat, ensuring integration of regulatory, clinical, commercial and global medical perspectives. 

• Lead and development the U.S. Neuromuscular Medical Affairs team, including Medical Science Liaisons (MSLs). 

• Oversee the execution of medical education, scientific exchange, and non-registrational evidence-generation initiatives. 

• Act as a strategic thought partner across Medical Affairs, R&D, and commercial teams. 

• Provide medical and scientific support for late-stage clinical development programs, ensuring alignment with business and regulatory strategies. 

• Support training and development of internal teams on product science and disease education. 

• Implement right-sized systems and processes to optimize effectiveness of the medical affairs neurometabolic organization 

• Establish and maintain strong, trusted relationships with external medical experts, academic institutions, and medical societies. 

• Oversee a comprehensive medical KOL engagement and insights-generation strategy. 

• Localize medical information and publication resources. 

• Develop medical governance frameworks to maintain high ethical and compliance standards in all engagements.

Required Skills:

• Advanced degree required (PharmD, MD, or PhD; PharmD strongly preferred). 

• Minimum 10 years of progressive experience in U.S. Medical Affairs within the pharmaceutical or biotechnology industry. 

• Prior leadership of cross-functional medical teams, including MSLs and medical communications. 

• Experience in rare diseases, neurology, or neuromuscular disorders is strongly preferred. 

• Deep knowledge of U.S. medical, regulatory, and pharmacovigilance standards. 

• Demonstrated ability to work in a fast-paced, evolving environment and to build highly effective and accountable teams from the ground up. 

• Experience supporting an early marketed product. 

• Collaborative and decisive leader with a proven ability to navigate and contribute effectively within a matrixed organization. 
• Exceptional interpersonal skills with a demonstrated ability to build strong relationships with both internal stakeholders and external partners. 

Additional Information: 

The base compensation range for this role is: $290,000 - $320,000. Compensation is determined through an analytical approach utilizing a combination of factors including, but not limited to, relevant skills & experience, job location, and internal equity.